
OpenAlex is a bibliographic catalogue of scientific papers, authors and institutions accessible in open access mode, named after the Library of Alexandria. It's citation coverage is excellent and I hope you will find utility in this listing of citing articles!
If you click the article title, you'll navigate to the article, as listed in CrossRef. If you click the Open Access links, you'll navigate to the "best Open Access location". Clicking the citation count will open this listing for that article. Lastly at the bottom of the page, you'll find basic pagination options.
Requested Article:
Erratum: Gene therapy for neurological disorders: progress and prospects
Benjamin E. Deverman, Bernard Ravina, Krystof S. Bankiewicz, et al.
Nature Reviews Drug Discovery (2018) Vol. 17, Iss. 10, pp. 767-767
Open Access | Times Cited: 251
Benjamin E. Deverman, Bernard Ravina, Krystof S. Bankiewicz, et al.
Nature Reviews Drug Discovery (2018) Vol. 17, Iss. 10, pp. 767-767
Open Access | Times Cited: 251
Showing 1-25 of 251 citing articles:
Adeno-associated virus vector as a platform for gene therapy delivery
Dan Wang, Phillip W.L. Tai, Guangping Gao
Nature Reviews Drug Discovery (2019) Vol. 18, Iss. 5, pp. 358-378
Open Access | Times Cited: 1838
Dan Wang, Phillip W.L. Tai, Guangping Gao
Nature Reviews Drug Discovery (2019) Vol. 18, Iss. 5, pp. 358-378
Open Access | Times Cited: 1838
Engineering adeno-associated virus vectors for gene therapy
Chengwen Li, R. Jude Samulski
Nature Reviews Genetics (2020) Vol. 21, Iss. 4, pp. 255-272
Closed Access | Times Cited: 938
Chengwen Li, R. Jude Samulski
Nature Reviews Genetics (2020) Vol. 21, Iss. 4, pp. 255-272
Closed Access | Times Cited: 938
Strategies for delivering therapeutics across the blood–brain barrier
Georg C. Terstappen, Axel H. Meyer, Robert D. Bell, et al.
Nature Reviews Drug Discovery (2021) Vol. 20, Iss. 5, pp. 362-383
Closed Access | Times Cited: 731
Georg C. Terstappen, Axel H. Meyer, Robert D. Bell, et al.
Nature Reviews Drug Discovery (2021) Vol. 20, Iss. 5, pp. 362-383
Closed Access | Times Cited: 731
Brain energy rescue: an emerging therapeutic concept for neurodegenerative disorders of ageing
Stephen C. Cunnane, Eugenia Trushina, Cecilie Morland, et al.
Nature Reviews Drug Discovery (2020) Vol. 19, Iss. 9, pp. 609-633
Open Access | Times Cited: 689
Stephen C. Cunnane, Eugenia Trushina, Cecilie Morland, et al.
Nature Reviews Drug Discovery (2020) Vol. 19, Iss. 9, pp. 609-633
Open Access | Times Cited: 689
Nanodelivery of nucleic acids
Bárbara B. Mendes, João Conniot, Aviram Avital, et al.
Nature Reviews Methods Primers (2022) Vol. 2, Iss. 1
Open Access | Times Cited: 394
Bárbara B. Mendes, João Conniot, Aviram Avital, et al.
Nature Reviews Methods Primers (2022) Vol. 2, Iss. 1
Open Access | Times Cited: 394
Next-generation regulatory T cell therapy
Leonardo M. R. Ferreira, Yannick D. Müller, Jeffrey A. Bluestone, et al.
Nature Reviews Drug Discovery (2019) Vol. 18, Iss. 10, pp. 749-769
Open Access | Times Cited: 392
Leonardo M. R. Ferreira, Yannick D. Müller, Jeffrey A. Bluestone, et al.
Nature Reviews Drug Discovery (2019) Vol. 18, Iss. 10, pp. 749-769
Open Access | Times Cited: 392
Therapeutic AAV Gene Transfer to the Nervous System: A Clinical Reality
Eloïse Hudry, Luk H. Vandenberghe
Neuron (2019) Vol. 101, Iss. 5, pp. 839-862
Open Access | Times Cited: 309
Eloïse Hudry, Luk H. Vandenberghe
Neuron (2019) Vol. 101, Iss. 5, pp. 839-862
Open Access | Times Cited: 309
Therapeutic in vivo delivery of gene editing agents
Aditya Raguram, Samagya Banskota, David R. Liu
Cell (2022) Vol. 185, Iss. 15, pp. 2806-2827
Open Access | Times Cited: 297
Aditya Raguram, Samagya Banskota, David R. Liu
Cell (2022) Vol. 185, Iss. 15, pp. 2806-2827
Open Access | Times Cited: 297
Therapies for rare diseases: therapeutic modalities, progress and challenges ahead
Erik Tambuyzer, Benjamin Vandendriessche, Christopher P. Austin, et al.
Nature Reviews Drug Discovery (2019) Vol. 19, Iss. 2, pp. 93-111
Open Access | Times Cited: 271
Erik Tambuyzer, Benjamin Vandendriessche, Christopher P. Austin, et al.
Nature Reviews Drug Discovery (2019) Vol. 19, Iss. 2, pp. 93-111
Open Access | Times Cited: 271
Genetics of amyotrophic lateral sclerosis: A review
Stéphane Mathis, Cyril Goizet, Antoine Soulages, et al.
Journal of the Neurological Sciences (2019) Vol. 399, pp. 217-226
Open Access | Times Cited: 223
Stéphane Mathis, Cyril Goizet, Antoine Soulages, et al.
Journal of the Neurological Sciences (2019) Vol. 399, pp. 217-226
Open Access | Times Cited: 223
Viral manipulation of functionally distinct interneurons in mice, non-human primates and humans
Douglas Vormstein-Schneider, Jessica Lin, Kenneth A. Pelkey, et al.
Nature Neuroscience (2020) Vol. 23, Iss. 12, pp. 1629-1636
Open Access | Times Cited: 208
Douglas Vormstein-Schneider, Jessica Lin, Kenneth A. Pelkey, et al.
Nature Neuroscience (2020) Vol. 23, Iss. 12, pp. 1629-1636
Open Access | Times Cited: 208
Strategies for enhancing cancer chemodynamic therapy performance
Deblin Jana, Yanli Zhao
Exploration (2022) Vol. 2, Iss. 2
Open Access | Times Cited: 199
Deblin Jana, Yanli Zhao
Exploration (2022) Vol. 2, Iss. 2
Open Access | Times Cited: 199
The GPI-Linked Protein LY6A Drives AAV-PHP.B Transport across the Blood-Brain Barrier
Juliette Hordeaux, Yuan Yuan, Peter Clark, et al.
Molecular Therapy (2019) Vol. 27, Iss. 5, pp. 912-921
Open Access | Times Cited: 187
Juliette Hordeaux, Yuan Yuan, Peter Clark, et al.
Molecular Therapy (2019) Vol. 27, Iss. 5, pp. 912-921
Open Access | Times Cited: 187
Gene therapy for neurodegenerative disorders: advances, insights and prospects
Wei Chen, Yang Hu, Dianwen Ju
Acta Pharmaceutica Sinica B (2020) Vol. 10, Iss. 8, pp. 1347-1359
Open Access | Times Cited: 159
Wei Chen, Yang Hu, Dianwen Ju
Acta Pharmaceutica Sinica B (2020) Vol. 10, Iss. 8, pp. 1347-1359
Open Access | Times Cited: 159
Multiplexed Cre-dependent selection yields systemic AAVs for targeting distinct brain cell types
Sripriya Ravindra Kumar, Timothy F. Miles, Xinhong Chen, et al.
Nature Methods (2020) Vol. 17, Iss. 5, pp. 541-550
Open Access | Times Cited: 153
Sripriya Ravindra Kumar, Timothy F. Miles, Xinhong Chen, et al.
Nature Methods (2020) Vol. 17, Iss. 5, pp. 541-550
Open Access | Times Cited: 153
Development of Novel Therapeutics Targeting the Blood–Brain Barrier: From Barrier to Carrier
Jia Li, Meng Zheng, Olga Shimoni, et al.
Advanced Science (2021) Vol. 8, Iss. 16
Open Access | Times Cited: 133
Jia Li, Meng Zheng, Olga Shimoni, et al.
Advanced Science (2021) Vol. 8, Iss. 16
Open Access | Times Cited: 133
Astrocyte-targeted gene delivery of interleukin 2 specifically increases brain-resident regulatory T cell numbers and protects against pathological neuroinflammation
Lidia Yshii, Emanuela Pasciuto, Pascal Bielefeld, et al.
Nature Immunology (2022) Vol. 23, Iss. 6, pp. 878-891
Open Access | Times Cited: 121
Lidia Yshii, Emanuela Pasciuto, Pascal Bielefeld, et al.
Nature Immunology (2022) Vol. 23, Iss. 6, pp. 878-891
Open Access | Times Cited: 121
Efficient in vivo base editing via single adeno-associated viruses with size-optimized genomes encoding compact adenine base editors
Jessie R. Davis, Xiao Wang, Isaac P. Witte, et al.
Nature Biomedical Engineering (2022) Vol. 6, Iss. 11, pp. 1272-1283
Open Access | Times Cited: 121
Jessie R. Davis, Xiao Wang, Isaac P. Witte, et al.
Nature Biomedical Engineering (2022) Vol. 6, Iss. 11, pp. 1272-1283
Open Access | Times Cited: 121
Stem Cell-Derived Exosomes: a New Strategy of Neurodegenerative Disease Treatment
Nashmin Fayazi Hosseini, Mohsen Sheykhhasan, Sara Soleimani Asl, et al.
Molecular Neurobiology (2021) Vol. 58, Iss. 7, pp. 3494-3514
Open Access | Times Cited: 114
Nashmin Fayazi Hosseini, Mohsen Sheykhhasan, Sara Soleimani Asl, et al.
Molecular Neurobiology (2021) Vol. 58, Iss. 7, pp. 3494-3514
Open Access | Times Cited: 114
AAV-based in vivo gene therapy for neurological disorders
Qinglan Ling, Jessica A. Herstine, Allison M. Bradbury, et al.
Nature Reviews Drug Discovery (2023) Vol. 22, Iss. 10, pp. 789-806
Closed Access | Times Cited: 93
Qinglan Ling, Jessica A. Herstine, Allison M. Bradbury, et al.
Nature Reviews Drug Discovery (2023) Vol. 22, Iss. 10, pp. 789-806
Closed Access | Times Cited: 93
Engineered AAVs for non-invasive gene delivery to rodent and non-human primate nervous systems
Xinhong Chen, Sripriya Ravindra Kumar, Cameron D. Adams, et al.
Neuron (2022) Vol. 110, Iss. 14, pp. 2242-2257.e6
Open Access | Times Cited: 91
Xinhong Chen, Sripriya Ravindra Kumar, Cameron D. Adams, et al.
Neuron (2022) Vol. 110, Iss. 14, pp. 2242-2257.e6
Open Access | Times Cited: 91
On-demand cell-autonomous gene therapy for brain circuit disorders
Yichen Qiu, Nathanael O’Neill, Benito Maffei, et al.
Science (2022) Vol. 378, Iss. 6619, pp. 523-532
Open Access | Times Cited: 76
Yichen Qiu, Nathanael O’Neill, Benito Maffei, et al.
Science (2022) Vol. 378, Iss. 6619, pp. 523-532
Open Access | Times Cited: 76
TRIM11 protects against tauopathies and is down-regulated in Alzheimer’s disease
Z. Zhang, Dilshan S. Harischandra, Ruifang Wang, et al.
Science (2023) Vol. 381, Iss. 6656
Open Access | Times Cited: 58
Z. Zhang, Dilshan S. Harischandra, Ruifang Wang, et al.
Science (2023) Vol. 381, Iss. 6656
Open Access | Times Cited: 58
Machine-guided design of cell-type-targeting cis-regulatory elements
Sager J. Gosai, Rodrigo Castro, Natalia Fuentes, et al.
Nature (2024) Vol. 634, Iss. 8036, pp. 1211-1220
Open Access | Times Cited: 26
Sager J. Gosai, Rodrigo Castro, Natalia Fuentes, et al.
Nature (2024) Vol. 634, Iss. 8036, pp. 1211-1220
Open Access | Times Cited: 26