
OpenAlex is a bibliographic catalogue of scientific papers, authors and institutions accessible in open access mode, named after the Library of Alexandria. It's citation coverage is excellent and I hope you will find utility in this listing of citing articles!
If you click the article title, you'll navigate to the article, as listed in CrossRef. If you click the Open Access links, you'll navigate to the "best Open Access location". Clicking the citation count will open this listing for that article. Lastly at the bottom of the page, you'll find basic pagination options.
Requested Article:
Base editing repairs an SGCA mutation in human primary muscle stem cells
Helena Escobar, Anne Krause, Sandra Keiper, et al.
JCI Insight (2021) Vol. 6, Iss. 10
Open Access | Times Cited: 21
Helena Escobar, Anne Krause, Sandra Keiper, et al.
JCI Insight (2021) Vol. 6, Iss. 10
Open Access | Times Cited: 21
Showing 21 citing articles:
Sarcoglycanopathies: an update
Mariz Vainzof, Lucas Santos Souza, Juliana Gurgel‐Giannetti, et al.
Neuromuscular Disorders (2021) Vol. 31, Iss. 10, pp. 1021-1027
Open Access | Times Cited: 37
Mariz Vainzof, Lucas Santos Souza, Juliana Gurgel‐Giannetti, et al.
Neuromuscular Disorders (2021) Vol. 31, Iss. 10, pp. 1021-1027
Open Access | Times Cited: 37
mRNA-mediated delivery of gene editing tools to human primary muscle stem cells
Christian Stadelmann, Silvia Di Francescantonio, Andreas Marg, et al.
Molecular Therapy — Nucleic Acids (2022) Vol. 28, pp. 47-57
Open Access | Times Cited: 23
Christian Stadelmann, Silvia Di Francescantonio, Andreas Marg, et al.
Molecular Therapy — Nucleic Acids (2022) Vol. 28, pp. 47-57
Open Access | Times Cited: 23
Advanced therapeutic approaches in sarcoglycanopathies
Martina Scano, Alberto Benetollo, Francesco Dalla Barba, et al.
Current Opinion in Pharmacology (2024) Vol. 76, pp. 102459-102459
Open Access | Times Cited: 5
Martina Scano, Alberto Benetollo, Francesco Dalla Barba, et al.
Current Opinion in Pharmacology (2024) Vol. 76, pp. 102459-102459
Open Access | Times Cited: 5
P2X7 Receptor Antagonist Reduces Fibrosis and Inflammation in a Mouse Model of Alpha-Sarcoglycan Muscular Dystrophy
Lizzia Raffaghello, Elisa Principi, Serena Baratto, et al.
Pharmaceuticals (2022) Vol. 15, Iss. 1, pp. 89-89
Open Access | Times Cited: 18
Lizzia Raffaghello, Elisa Principi, Serena Baratto, et al.
Pharmaceuticals (2022) Vol. 15, Iss. 1, pp. 89-89
Open Access | Times Cited: 18
Gene-editing in patient and humanized-mice primary muscle stem cells rescues dysferlin expression in dysferlin-deficient muscular dystrophy
Helena Escobar, Silvia Di Francescantonio, Julia Smirnova, et al.
Nature Communications (2025) Vol. 16, Iss. 1
Open Access
Helena Escobar, Silvia Di Francescantonio, Julia Smirnova, et al.
Nature Communications (2025) Vol. 16, Iss. 1
Open Access
Myogenic Cell Transplantation in Genetic and Acquired Diseases of Skeletal Muscle
Olivier Boyer, Gillian Butler‐Browne, Hector Chinoy, et al.
Frontiers in Genetics (2021) Vol. 12
Open Access | Times Cited: 22
Olivier Boyer, Gillian Butler‐Browne, Hector Chinoy, et al.
Frontiers in Genetics (2021) Vol. 12
Open Access | Times Cited: 22
Cas9-induced single cut enables highly efficient and template-free repair of a muscular dystrophy causing founder mutation
Stefanie Müthel, Andreas Marg, Busem Ignak, et al.
Molecular Therapy — Nucleic Acids (2023) Vol. 31, pp. 494-511
Open Access | Times Cited: 7
Stefanie Müthel, Andreas Marg, Busem Ignak, et al.
Molecular Therapy — Nucleic Acids (2023) Vol. 31, pp. 494-511
Open Access | Times Cited: 7
The Promises and Pitfalls of CRISPR-Mediated Base Editing in Stem Cells
Poh Kuan Wong, Nurul Nadia Mohamad Zamberi, Saiful Effendi Syafruddin, et al.
The CRISPR Journal (2023) Vol. 6, Iss. 3, pp. 196-215
Closed Access | Times Cited: 6
Poh Kuan Wong, Nurul Nadia Mohamad Zamberi, Saiful Effendi Syafruddin, et al.
The CRISPR Journal (2023) Vol. 6, Iss. 3, pp. 196-215
Closed Access | Times Cited: 6
An Update of Clinical, Epidemiological, and Psychosocial Features in Gamma-Sarcoglycanopathy
Naoufel Chabbi, C. Angelini, Alicia Aurora Rodríguez
Muscles (2023) Vol. 2, Iss. 2, pp. 164-176
Open Access | Times Cited: 5
Naoufel Chabbi, C. Angelini, Alicia Aurora Rodríguez
Muscles (2023) Vol. 2, Iss. 2, pp. 164-176
Open Access | Times Cited: 5
Generation of hiPSC-Derived Skeletal Muscle Cells: Exploiting the Potential of Skeletal Muscle-Derived hiPSCs
Eric Metzler, Helena Escobar, Daniele Yumi Sunaga, et al.
Biomedicines (2022) Vol. 10, Iss. 5, pp. 1204-1204
Open Access | Times Cited: 4
Eric Metzler, Helena Escobar, Daniele Yumi Sunaga, et al.
Biomedicines (2022) Vol. 10, Iss. 5, pp. 1204-1204
Open Access | Times Cited: 4
Aberrant Adenosine Triphosphate Release and Impairment of P2Y2-Mediated Signaling in Sarcoglycanopathies
Andrea Benzi, Serena Baratto, Cecilia Astigiano, et al.
Laboratory Investigation (2023) Vol. 103, Iss. 3, pp. 100037-100037
Open Access | Times Cited: 2
Andrea Benzi, Serena Baratto, Cecilia Astigiano, et al.
Laboratory Investigation (2023) Vol. 103, Iss. 3, pp. 100037-100037
Open Access | Times Cited: 2
“suMus,” a novel digital system for arm movement metrics and muscle energy expenditure
Teresa Gerhalter, Christina Müller, Elke Maron, et al.
Frontiers in Physiology (2023) Vol. 14
Open Access | Times Cited: 2
Teresa Gerhalter, Christina Müller, Elke Maron, et al.
Frontiers in Physiology (2023) Vol. 14
Open Access | Times Cited: 2
Recent Research Trends in Stem Cells Using CRISPR/Cas-Based Genome Editing Methods
Da Eun Yoon, Hyunji Lee, Kyoungmi Kim
International Journal of Stem Cells (2023) Vol. 17, Iss. 1, pp. 1-14
Open Access | Times Cited: 2
Da Eun Yoon, Hyunji Lee, Kyoungmi Kim
International Journal of Stem Cells (2023) Vol. 17, Iss. 1, pp. 1-14
Open Access | Times Cited: 2
Prinzipien der translationalen Gentherapie für neuromuskuläre Erkrankungen
Benedikt Schoser
Der Nervenarzt (2022) Vol. 93, Iss. 6, pp. 537-548
Closed Access | Times Cited: 3
Benedikt Schoser
Der Nervenarzt (2022) Vol. 93, Iss. 6, pp. 537-548
Closed Access | Times Cited: 3
Autosomal Recessive Limb-Girdle Muscular Dystrophy-3: A Case Report of a Patient with Autism Spectrum Disorder
Sivan Lewis, Amy Woroch, Mary Kate Hatch, et al.
Genes (2023) Vol. 14, Iss. 8, pp. 1587-1587
Open Access | Times Cited: 1
Sivan Lewis, Amy Woroch, Mary Kate Hatch, et al.
Genes (2023) Vol. 14, Iss. 8, pp. 1587-1587
Open Access | Times Cited: 1
En route towards a personalized medicine approach: Innovative therapeutic modalities for connective tissue disorders
Charlene Redhead, Nandaraj Taye, Dirk Hubmacher
Matrix Biology (2023) Vol. 122, pp. 46-54
Open Access | Times Cited: 1
Charlene Redhead, Nandaraj Taye, Dirk Hubmacher
Matrix Biology (2023) Vol. 122, pp. 46-54
Open Access | Times Cited: 1
Gene-edited primary muscle stem cells rescue dysferlin-deficient muscular dystrophy
Helena Escobar, Silvia Di Francescantonio, Andreas Marg, et al.
bioRxiv (Cold Spring Harbor Laboratory) (2024)
Open Access
Helena Escobar, Silvia Di Francescantonio, Andreas Marg, et al.
bioRxiv (Cold Spring Harbor Laboratory) (2024)
Open Access
Single-cell RNA sequencing unveils the activation of EGR1-ATF3 signaling in EGR1 + muscle stem cells during human paravertebral muscle degeneration
Yongjin Li, Baobao Wang, Wenzhi Sun, et al.
Materials & Design (2024) Vol. 242, pp. 113027-113027
Open Access
Yongjin Li, Baobao Wang, Wenzhi Sun, et al.
Materials & Design (2024) Vol. 242, pp. 113027-113027
Open Access
LMNA Co-Regulated Gene Expression as a Suitable Readout after Precise Gene Correction
Haicui Wang, Anne Krause, Helena Escobar, et al.
International Journal of Molecular Sciences (2022) Vol. 23, Iss. 24, pp. 15525-15525
Open Access | Times Cited: 1
Haicui Wang, Anne Krause, Helena Escobar, et al.
International Journal of Molecular Sciences (2022) Vol. 23, Iss. 24, pp. 15525-15525
Open Access | Times Cited: 1
Messenger RNA brings gene editing a step closer to treat muscular dystrophies
John Jacob
Molecular Therapy — Nucleic Acids (2022) Vol. 28, pp. 462-463
Open Access
John Jacob
Molecular Therapy — Nucleic Acids (2022) Vol. 28, pp. 462-463
Open Access
Stammzelltherapien für Muskeldystrophien
Helena Escobar
BIOspektrum (2022) Vol. 28, Iss. 5, pp. 493-496
Open Access
Helena Escobar
BIOspektrum (2022) Vol. 28, Iss. 5, pp. 493-496
Open Access