
OpenAlex is a bibliographic catalogue of scientific papers, authors and institutions accessible in open access mode, named after the Library of Alexandria. It's citation coverage is excellent and I hope you will find utility in this listing of citing articles!
If you click the article title, you'll navigate to the article, as listed in CrossRef. If you click the Open Access links, you'll navigate to the "best Open Access location". Clicking the citation count will open this listing for that article. Lastly at the bottom of the page, you'll find basic pagination options.
Requested Article:
Towards Personalized Allele-Specific Antisense Oligonucleotide Therapies for Toxic Gain-of-Function Neurodegenerative Diseases
Jacob Helm, Lüdger Schöls, Stefan Hauser
Pharmaceutics (2022) Vol. 14, Iss. 8, pp. 1708-1708
Open Access | Times Cited: 34
Jacob Helm, Lüdger Schöls, Stefan Hauser
Pharmaceutics (2022) Vol. 14, Iss. 8, pp. 1708-1708
Open Access | Times Cited: 34
Showing 1-25 of 34 citing articles:
Possibilities and limitations of antisense oligonucleotide therapies for the treatment of monogenic disorders
Marlen C. Lauffer, Willeke M. C. van Roon‐Mom, Annemieke Aartsma‐Rus
Communications Medicine (2024) Vol. 4, Iss. 1
Open Access | Times Cited: 81
Marlen C. Lauffer, Willeke M. C. van Roon‐Mom, Annemieke Aartsma‐Rus
Communications Medicine (2024) Vol. 4, Iss. 1
Open Access | Times Cited: 81
Integrating non-mammalian model organisms in the diagnosis of rare genetic diseases in humans
Shinya Yamamoto, Oguz Kanca, Michael F. Wangler, et al.
Nature Reviews Genetics (2023) Vol. 25, Iss. 1, pp. 46-60
Closed Access | Times Cited: 42
Shinya Yamamoto, Oguz Kanca, Michael F. Wangler, et al.
Nature Reviews Genetics (2023) Vol. 25, Iss. 1, pp. 46-60
Closed Access | Times Cited: 42
Nucleic Acid Therapeutics: Successes, Milestones, and Upcoming Innovation
Jillian Belgrad, Hassan H. Fakih, Anastasia Khvorova
Nucleic Acid Therapeutics (2024) Vol. 34, Iss. 2, pp. 52-72
Closed Access | Times Cited: 33
Jillian Belgrad, Hassan H. Fakih, Anastasia Khvorova
Nucleic Acid Therapeutics (2024) Vol. 34, Iss. 2, pp. 52-72
Closed Access | Times Cited: 33
Nucleic acid drugs: recent progress and future perspectives
Xiaoyi Sun, Sarra Setrerrahmane, Chencheng Li, et al.
Signal Transduction and Targeted Therapy (2024) Vol. 9, Iss. 1
Open Access | Times Cited: 11
Xiaoyi Sun, Sarra Setrerrahmane, Chencheng Li, et al.
Signal Transduction and Targeted Therapy (2024) Vol. 9, Iss. 1
Open Access | Times Cited: 11
Exploring human biology with N-of-1 clinical trials
Nicholas J. Schork, Brett K. Beaulieu‐Jones, Winnie S. Liang, et al.
Cambridge Prisms Precision Medicine (2023) Vol. 1
Open Access | Times Cited: 16
Nicholas J. Schork, Brett K. Beaulieu‐Jones, Winnie S. Liang, et al.
Cambridge Prisms Precision Medicine (2023) Vol. 1
Open Access | Times Cited: 16
Mechanisms underlying phenotypic variation in neurogenetic disorders
Jean‐Marc Burgunder
Nature Reviews Neurology (2023) Vol. 19, Iss. 6, pp. 363-370
Closed Access | Times Cited: 11
Jean‐Marc Burgunder
Nature Reviews Neurology (2023) Vol. 19, Iss. 6, pp. 363-370
Closed Access | Times Cited: 11
Strategies to improve the design of gapmer antisense oligonucleotide on allele-specific silencing
Sara Aguti, Shuzhi Cheng, Pierpaolo Ala, et al.
Molecular Therapy — Nucleic Acids (2024) Vol. 35, Iss. 3, pp. 102237-102237
Open Access | Times Cited: 4
Sara Aguti, Shuzhi Cheng, Pierpaolo Ala, et al.
Molecular Therapy — Nucleic Acids (2024) Vol. 35, Iss. 3, pp. 102237-102237
Open Access | Times Cited: 4
Design and Preliminary Screen of Antisense Oligonucleotides
Nofar Mor, Sharon Avkin-Nachum, Dan Dominissini
Methods in molecular biology (2025), pp. 51-61
Closed Access
Nofar Mor, Sharon Avkin-Nachum, Dan Dominissini
Methods in molecular biology (2025), pp. 51-61
Closed Access
An inclusive study of recent advancements in Alzheimer's disease: A comprehensive review
Sukanya Singh, Mitali Mahajan, D. Renjith Kumar, et al.
Neuropeptides (2023) Vol. 102, pp. 102369-102369
Closed Access | Times Cited: 8
Sukanya Singh, Mitali Mahajan, D. Renjith Kumar, et al.
Neuropeptides (2023) Vol. 102, pp. 102369-102369
Closed Access | Times Cited: 8
Blood and cerebellar abundance of ATXN3 splice variants in spinocerebellar ataxia type 3/Machado-Joseph disease
Mafalda Raposo, Jeannette Hübener‐Schmid, Rebecca Tagett, et al.
Neurobiology of Disease (2024) Vol. 193, pp. 106456-106456
Open Access | Times Cited: 2
Mafalda Raposo, Jeannette Hübener‐Schmid, Rebecca Tagett, et al.
Neurobiology of Disease (2024) Vol. 193, pp. 106456-106456
Open Access | Times Cited: 2
Gene therapy for the leukodystrophies: From preclinical animal studies to clinical trials
Jasna Metović, Yedda Li, Yi Gong, et al.
Neurotherapeutics (2024) Vol. 21, Iss. 4, pp. e00443-e00443
Open Access | Times Cited: 2
Jasna Metović, Yedda Li, Yi Gong, et al.
Neurotherapeutics (2024) Vol. 21, Iss. 4, pp. e00443-e00443
Open Access | Times Cited: 2
Influence of Combinations of Lipophilic and Phosphate Backbone Modifications on Cellular Uptake of Modified Oligonucleotides
Timofey D. Zharkov, Oleg V. Markov, Sergey A. Zhukov, et al.
Molecules (2024) Vol. 29, Iss. 2, pp. 452-452
Open Access | Times Cited: 1
Timofey D. Zharkov, Oleg V. Markov, Sergey A. Zhukov, et al.
Molecules (2024) Vol. 29, Iss. 2, pp. 452-452
Open Access | Times Cited: 1
Translatome analysis in acute ischemic stroke: Astrocytes and microglia exhibit differences in poststroke alternative splicing of expressed transcripts
Bingxue Jin, Yilai Han, Fang Xu, et al.
The FASEB Journal (2024) Vol. 38, Iss. 15
Open Access | Times Cited: 1
Bingxue Jin, Yilai Han, Fang Xu, et al.
The FASEB Journal (2024) Vol. 38, Iss. 15
Open Access | Times Cited: 1
Tofersen for SOD1 ALS
William Everett, Robert C. Bucelli
Neurodegenerative Disease Management (2024) Vol. 14, Iss. 5, pp. 149-160
Open Access | Times Cited: 1
William Everett, Robert C. Bucelli
Neurodegenerative Disease Management (2024) Vol. 14, Iss. 5, pp. 149-160
Open Access | Times Cited: 1
CRISPR/Cas9-generated mouse model with humanizing single-base substitution in the Gnao1 for safety studies of RNA therapeutics
Anna V. Polikarpova, Tatiana V. Egorova, Evgenii A. Lunev, et al.
Frontiers in Genome Editing (2023) Vol. 5
Open Access | Times Cited: 3
Anna V. Polikarpova, Tatiana V. Egorova, Evgenii A. Lunev, et al.
Frontiers in Genome Editing (2023) Vol. 5
Open Access | Times Cited: 3
Influence of Combinations of Lipophilic and Phosphate Backbone Modifications on Cellular Uptake of Modified Oligonucleotides
Timofey D. Zharkov, Oleg V. Markov, Sergey A. Zhukov, et al.
(2023)
Open Access | Times Cited: 2
Timofey D. Zharkov, Oleg V. Markov, Sergey A. Zhukov, et al.
(2023)
Open Access | Times Cited: 2
Genetics of Huntington’s disease and related disorders: beyond triplet repeats
Jean‐Marc Burgunder
Ageing and Neurodegenerative Diseases (2024)
Open Access
Jean‐Marc Burgunder
Ageing and Neurodegenerative Diseases (2024)
Open Access
Treatability of the KMT2-Associated Neurodevelopmental Disorders Using Antisense Oligonucleotide-Based Treatments
Bianca Zardetto, Willeke M. C. van Roon‐Mom, Annemieke Aartsma‐Rus, et al.
Human Mutation (2024) Vol. 2024, pp. 1-17
Open Access
Bianca Zardetto, Willeke M. C. van Roon‐Mom, Annemieke Aartsma‐Rus, et al.
Human Mutation (2024) Vol. 2024, pp. 1-17
Open Access
The threats and therapeutics of neurodegenerative disorders: A commentary
Samudra Prosad Banik, Debasis Bagchi
Elsevier eBooks (2024), pp. 679-685
Closed Access
Samudra Prosad Banik, Debasis Bagchi
Elsevier eBooks (2024), pp. 679-685
Closed Access
Review of the Use of Antisense Oligonucleotides as Therapy for Huntington's Disease
Ariel Solis-Chiriboga, Alberto Bustillos
Salud Ciencia y Tecnología - Serie de Conferencias (2024) Vol. 3, pp. 923-923
Open Access
Ariel Solis-Chiriboga, Alberto Bustillos
Salud Ciencia y Tecnología - Serie de Conferencias (2024) Vol. 3, pp. 923-923
Open Access
Review of the Use of Antisense Oligonucleotides as Therapy for Huntington's Disease
Ariel Solis-Chiriboga, Alberto Bustillos
Salud Ciencia y Tecnología - Serie de Conferencias (2024) Vol. 3, pp. 795-795
Open Access
Ariel Solis-Chiriboga, Alberto Bustillos
Salud Ciencia y Tecnología - Serie de Conferencias (2024) Vol. 3, pp. 795-795
Open Access
Mendelian, non-Mendelian, multigenic inheritance, and epigenetics
Tamar Harel, James R. Lupski
Elsevier eBooks (2024), pp. 3-27
Closed Access
Tamar Harel, James R. Lupski
Elsevier eBooks (2024), pp. 3-27
Closed Access
Blood and cerebellar abundance ofATXN3splice variants in spinocerebellar ataxia type 3/Machado-Joseph disease
Mafalda Raposo, Jeannette Hübener‐Schmid, Rebecca Tagett, et al.
bioRxiv (Cold Spring Harbor Laboratory) (2023)
Open Access | Times Cited: 1
Mafalda Raposo, Jeannette Hübener‐Schmid, Rebecca Tagett, et al.
bioRxiv (Cold Spring Harbor Laboratory) (2023)
Open Access | Times Cited: 1
Review: EXPLORING HUMAN BIOLOGY WITH N-OF-1 CLINICAL TRIALS — R0/PR3
Nicholas J. Schork, Brett K. Beaulieu‐Jones, Winnie S. Liang, et al.
(2022)
Open Access
Nicholas J. Schork, Brett K. Beaulieu‐Jones, Winnie S. Liang, et al.
(2022)
Open Access